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A baby born with a rare and dangerous genetic disease is thriving after getting an experimental gene editing treatment made just for him. Researchers said the Pennsylvania boy is among the first to be successfully treated with a custom gene editing therapy. They described his case in a study published on Thursday in the New England Journal of Medicine. Though it may be a while before similar personalized treatments are available for others, doctors hope the technology can someday help millions who have been left behind by genetic medicine because their diseases are so rare.

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This photo provided by the Children's Hospital of Philadelphia shows KJ Muldoon after a follow up dose of an experimental gene editing treatment at the hospital in April 2025. (Chloe Dawson/Children's Hospital of Philadelphia via AP)

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In this photo provided by the Children's Hospital of Philadelphia, KJ Muldoon, center, sits with his siblings after a follow up dose of an experimental gene editing treatment at the hospital in April 2025. (Chloe Dawson/Children's Hospital of Philadelphia via AP)

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In this photo provided by the Children's Hospital of Philadelphia, Drs. Kiran Musunuru, left, and Rebecca Ahrens-Nicklas stand with KJ Muldoon, center, after a follow up dose of an experimental gene editing treatment at the hospital in April 2025. (Chloe Dawson/Children's Hospital of Philadelphia via AP)

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In this photo provided by the Children's Hospital of Philadelphia, KJ Muldoon sits with his parents, Kyle and Nicole Muldoon, and his siblings after a follow up dose of an experimental gene editing treatment at the hospital in April 2025. (Chloe Dawson/Children's Hospital of Philadelphia via AP)

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President Donald Trump性视界传媒檚 new pick for surgeon general wrote in a recent book that people should consider using unproven psychedelic drugs as therapy and in a newsletter suggested her use of mushrooms helped her find love. Dr. Casey Means性视界传媒 recommendation to consider guided psilocybin-assisted therapy is notable because psilocybin is illegal under federal law. The surgeon general性视界传媒檚 job is to provide Americans with the best scientific information available on how to improve their health. Means made the recommendation in her 2024 book, 性视界传媒淕ood Energy.性视界传媒 Means received her undergraduate and medical degrees from Stanford University and began a medical residency in Oregon but didn't complete it. Means has declined to comment.